The invention relates to a method of treating ocular amyloidosis by reducing TTR expression in a subject by administering a double-stranded ribonucleic acid (dsRNA) that targets a TTR gene to the retinal pigment epithelium of the subject.
本发明涉及一种治疗眼部淀粉样变性的方法,通过向受试者的视网膜色素上皮细胞注射靶向
TTR
基因的双链
核糖核酸(dsRNA),从而降低受试者的
TTR表达。